Batten Disease and Gene Therapy
Вставка
- Опубліковано 15 жов 2024
- Batten disease occurs when at least one of the thirteen known ceroid lipofuscinosis (CLN) genes is mutated. Gene therapy may offer a one-time treatment to slow or ideally stop the progression of these disorders by delivering a working gene to target the cause of the disease.
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Thanks for the video! It makes it easy for those without a medical background to follow. My niece has Batten's ... praying for that gene therapy!! 💜🦋
How is she doing
I hope and pray this works for your niece. I just saw Love, Kennedy and this disease has me in a tizzy. I'm so saddened and truly hope this works. Truly!
😱 omg, it's happening already... congratulation "Jennifer Doudna".
Marissa, what's happening already???
@@bigmoneygrip6561 What’s happening is it sounds like they’re close to a cure for Barton’s disease.
This is where AI technology will really excel at treating a disease.
How do I connect with these people we just found out my daughter has a malfunctioning cnl3 receptor and is going to go through this
My son has cln6 and is getting enzyme therapy
@@aaliyahali3314Hey. Is he really getting gene therapy? I heard only cln2 has approved gene therapy.
Keep up the work on this terrible desisis
My sister has it
@@ollie4999 how is your sister doing she need stem cell and enzyme treatment
السلام عليكم هل من علاج لهذا المرض
السلام عليكم ورحمة الله وبركاته ممكن نتواصل ابنتي مريضة ب cln1
@@noflanofla3789 مرحبا
No sadly