Cystic Fibrosis Gene Therapy - Not As Easy as We Thought
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- Опубліковано 5 лют 2025
- The goal of cystic fibrosis gene therapy is to deliver genetic code for Cystic Fibrosis Transmembrane Regulator (CFTR) to lung epithelial cells. If a sufficient number of epithelial cells start producing functional CFTR protein, chloride ion transport and mucus clearing mechanisms in lungs will be restored
To learn more read the article on my web site: bio501.com/cys...
Complete article about cystic fibrosis gene therapy bio501.com/cystic-fibrosis-gene-therapy
Thanks for your work! Well explained. People like you make our world better place ! You are the best
Amazing! Fantastic! Incredible! Astonishing! It's much better than all of Marvel's movies!
I feel there is so much more that could be said concerning this. In 2016 they did manage to partially restore CFTR function to knock out mice. There are lots more issues with mRNA therapy than those listed here. It's also not true that carriers don't suffer. Carrier status of certain mutations is strongly linked to COPD for example. Lastly , what about therapies such as curcumin? These are known to improve both folding and transportation of the protein to the cell membrane.
Great presentation on CF, IV got CF too
Thankyou my friend
So great explanation
Sir me and husband are CFTR career...my first baby got CFTR ,she passed away when she was in 3 month....next I was conceived but I got cvs test,the result came that baby also affect CFTR..so we decided to terminate when I was 4 month pregnant..... really I getting fear about next pregnancy.... can it possible for normal or career babe without CFTR?
I in 4 chance of having a CF child if you are both carriers. Many carriers of the gene are now deciding to have IVF.
Thanks for ur reply