Iptacopan for Paroxysmal Nocturnal Hemoglobinuria | NEJM

Many patients with paroxysmal nocturnal hemoglobinuria have persistent anemia despite anti-C5
treatment. The efficacy and safety of the complement inhibitor iptacopan in PNH are unclear.
Research findings are summarized in a new Quick Take video.
To see the full article, follow this link: nej.md/48QKlcU
#hematology #oncology #clinicaltrials #medicalresearch #nejm