2023: year in review for Wilson disease

Speaker: Frederick Askari, MD, PhD - Wilson Disease Center of Excellence, Michigan Medicine
The past year has been an eventful one for the Wilson disease community. We’ve seen major steps forward with the first patients receiving gene therapy and the launch of a stable form of trientine as well as what may appear as a setback with the termination of a novel treatment. Dr. Askari puts these and other developments in perspective and describes the hope in emerging therapies and diagnostic tools.