The State of Gene Therapy in CMT
Вставка
- Опубліковано 24 жов 2023
- The pros and cons of gene therapy in CMT, highlighting its potential for targeted treatment, disease modification, and long-term benefits, alongside challenges like delivery methods, immune responses, and the importance of personalized approaches based on specific genetic mutations.
Afrooz Rashnonejad, MSc, PhD, Nationwide Children’s Hospital