Dravet Syndrome: Potential Role of Gene Regulation Therapy

Dravet syndrome is a severe, complex, lifelong disorder of the central nervous system, characterized by frequent, prolonged, and difficult-to-treat seizures, significant cognitive delays, sleep abnormalities, motor impairment, and profound behavioral difficulties. There are currently no approved therapies that address the full spectrum of manifestations associated with Dravet syndrome or the root cause of the disease, but there are types of gene therapy approaches that may offer hope. Learn more about gene regulation therapy and its potential role for treating Dravet syndrome.