Gene Therapy for Duchenne Muscular Dystrophy: Cash’s Story
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- Опубліковано 30 жов 2023
- Children’s Hospital of Philadelphia now offers the first-ever gene therapy treatment for Duchenne Muscular Dystrophy (DMD) to patients like 6-year-old Cash. This breakthrough treatment slows the progression of symptoms and can improve strength and endurance for patients with DMD.
- Наука та технологія
Great hope. Well done breakthrough makers
DEAR CASH & EVERYONE AT CHILDREN'S HOSPITAL OF PHILADELPHIA,
GOD BLESS YOU MY FRIENDS. I AM VERY PROUD OF YOU AND VERY HAPPY FOR YOU. I HOPE ALL OF YOUR DREAMS COME TRUE. 🙏
I LOVE YOU SO VERY MUCH. 🙏
GOD BLESS YOU SO VERY MUCH CASH. 🙏
I LOVE CHILDREN'S HOSPITAL OF PHILADELPHIA SO VERY MUCH. 🙏
SINCERELY PETER
My son 6 years was the same hospital with the same doctor he hase dmd too I hope God help all the kids and parent too
@@elmehdiamine9103 GOD BLESS YOUR SON. GOD BLESS ALL OF THE BEAUTIFUL DOCTORS. GOD BLESS ALL OF THE BEAUTIFUL PARENTS. GOD BLESS EVERYONE AT CHILDREN'S HOSPITAL OF PHILADELPHIA. I LOVE THE CHILDREN'S HOSPITAL OF PHILADELPHIA SO VERY MUCH. I WILL PRAY FOR EVERYONE. 🙏
How much does this cost?
Is there gene therapy for kcnq2 gene varients ??
Iam from Guyana my grandson is 10 years old he have dmd he is not walking we need help for him
My brothers son ( 13 years old ) having this but we dont have treatment in Sri Lanka.we need help and guide from youll.
Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6052YXeXr for additional information.
my son is 9 years old he is DMD patient (7 exon is deletion) in genetic report im in pakistan please help me 😢
I wish older children could get it I would give anything to stop my sons rate of progression I hate this disease so much
My son is ten year old with DMD I am from Mauritius .He stop walking since last year please help if there is any treatment let me know.
Hello. Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6052cRRYm for additional information.
I am from China. My son is DMD patient. He is 5 years old. Is it possible to cure? And how much would be the cost?❤
Hello. Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6052cRRYm for additional information.
@@ChildrensHospPhila Thanks for your feedback.I will check it out
Im from Srilanka .My son also suffering from DMD.now he's 8years old.still he is working slowly .please please help me if there is any possibility .thank tou .
Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6050Y6icC for additional information.
My sister's son in DMD exons 48-52 deletion.He is 2 year's 11 months old. please hlp me what is suitable treatment for him. I am form Punjab
Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6051YbU41 for additional information.
Did you get any treatment for your sister's son ? Plz tell if any
Yes great and all. I want to see results, of course I can find some results but I would like to see much more results and since what I have seen (have been shown?) are results within months we should be able to see these in more kids. Not just a few.
My son 2years 11month old affect in DMD (14 exon is deletion or duplication) in gentic report. Please help me what is suitable treatment for my baby ( i am in India) please..... share me
Hi madam for Duchenne Muscular Dystrophy and every type of Dystrophy can give treatment in Nimhans Hospital in Bangalore
Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6052iFuJk for additional information.
Exon 14 can be tricky, so inform yourself. I think 1-9 and 17 so 14 should in theory be fine but again ask your specialist.
14 exons (Exon 30 -43) deletion or duplication in genetic report
Wow good news
Successful Hope
Please help my son is suffering ducchne muscular dystrophy since 8 years please help 😭😭 I am from India
Hello. Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6052cRRYm for additional information.
Hi I'm edrian from Philippines my brother suffere DMD since 7yr.old please help my brother
Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6050ctwEo for additional information.
I'm from India am DMD patient I'm 21years old help me to cure 😢
Hi! Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6052cRRYm for additional information.
Hello . Can I get your contact no.
To explore treatment options at Children's Hospital of Philadelphia, please contact us at 1-800-879-2467 or visit our website ms.spr.ly/6054cmH3m.
Our sons have Duchenne. They are 10 and 13. Any help or hope for them?
Thank you for contacting us. To explore treatment options at Children's Hospital of Philadelphia, please contact us at 1-800-879-2467 or visit our website ms.spr.ly/6056cQTaa.