UnravelingRare Ep03: Stratifying AP-4 Spastic Paraplegias to Accelerate Therapies

In our third episode, we speak with Kasey Edwards, Community Relations Coordinator at the Cure AP-4 Foundation (cureap4.org/) and mother of a child with SPG47, one of the four genes that make up AP-4 spastic paraplegias. Learn about the foundation's incredible work to tackle four disorders at once by finding shared treatments among them and by linking these ultra-rare disorders to less rare, and more funded indications to accelerate the development of effective therapies.
www.rareshift....