An Overview of Gene Therapy in PKU

Lex Cowsert, Ph.D., NPKUA Director of Research Development, provides an overview of the goal of gene therapy and what to expect during the gene therapy trials. This is video 3 from our 6-part series on gene therapy to help PKU patients and the general public understand and demystify some of the concepts related to gene therapy in PKU. Don’t forget to read our 5-Year Scientific Strategic Plan www.npkua.org/..., the perfect complement to our gene therapy video series.

[@romanairdrop3137]

Very good video, thank you!