Antisense Oligonucleotides (ASO)
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- Опубліковано 12 жов 2022
- Describes Antisense Oligonucleotide (ASO) technology and how it can be used to treat a variety of genetic disorders with no previous effective conventional therapy. Spinal Muscular Atrophy (SMA) and Lipoprotein (a) or Lp(a) are presented as examples.
Very clear explanations- even for an old-non-biologist !
Thank you!
Fantastic!
Would this work on familial CJD with the E200K-129M mutation?
💯